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Publication
PropertyValue
Working Groups Klopstock
SubprojectNone
Open AccessOpen Access Yes
Publication TypeJournal Article
Peer ReviewedYes
PMIDPubMed ID 34853716
DOIDOI 10.1016/j.omtn.2021.10.019
Publication Year2021
TitleAutosomal dominant optic atrophy: A novel treatment for OPA1 splice defects using U1 snRNA adaption.
JournalMolecular therapy. Nucleic acids
ISSN2162-2531
ESSN2162-2531
URL https://www.ncbi.nlm.nih.gov/pubmed/?term=34853716%5Buid%5D
Pages1186-1197
Volume26
Journal AbbreviationMol Ther Nucleic Acids
AuthorsJüschke C, Klopstock T, Catarino CB, Owczarek-Lipska M, Wissinger B, Neidhardt J
First AuthorJüschke C
Last AuthorNeidhardt J