View publication

↩ Back to all publications
Publication
PropertyValue
Working Groups Behrends
SubprojectNone
Open AccessOpen Access Yes
Publication TypeJournal Article
Peer ReviewedYes
PMIDPubMed ID 35860385
DOIDOI 10.1016/j.omtn.2022.06.015
Publication Year2022
TitleDeveloping antisense oligonucleotides for a TECPR2 mutation-induced, ultra-rare neurological disorder using patient-derived cellular models.
JournalMolecular therapy. Nucleic acids
ISSN2162-2531
ESSN2162-2531
URL https://www.ncbi.nlm.nih.gov/pubmed/?term=35860385%5Buid%5D
Pages189-203
Volume29
Journal AbbreviationMol Ther Nucleic Acids
AuthorsWilliams LA, Gerber DJ, Elder A, Tseng WC, Baru V, Delaney-Busch N, Ambrosi C, Mahimkar G, Joshi V, Shah H, Harikrishnan K, Upadhyay H, Rajendran SH, Dhandapani A, Meier J, Ryan SJ, Lewarch C, Black L, Douville J, Cinquino S, Legakis H, Nalbach K, Behrends C, Sato A, Galluzzi L, Yu TW, Brown D, Agrawal S, Margulies D, Kopin A, Dempsey GT
First AuthorWilliams LA
Last AuthorDempsey GT