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Publication
PropertyValue
Working Groups Klopstock
SubprojectNone
Open AccessOpen Access Yes
Publication TypeJournal Article
Peer ReviewedYes
PMIDPubMed ID 36496192
DOIDOI 10.1016/j.ajo.2022.11.026
Publication Year2023
TitleSafety of Lenadogene Nolparvovec Gene Therapy Over 5 Years in 189 Patients With Leber Hereditary Optic Neuropathy.
JournalAmerican journal of ophthalmology
ISSN0002-9394
ESSN1879-1891
URL https://www.ncbi.nlm.nih.gov/pubmed/?term=36496192%5Buid%5D
Pages108-125
Volume249
Journal AbbreviationAm J Ophthalmol
AuthorsVignal-Clermont C, Yu-Wai-Man P, Newman NJ, Carelli V, Moster ML, Biousse V, Subramanian PS, Wang AG, Donahue SP, Leroy BP, Sadun AA, Klopstock T, Sergott RC, Rebolleda Fernandez G, Chwalisz BK, Banik R, Taiel M, Roux M, Sahel JA
First AuthorVignal-Clermont C
Last AuthorSahel JA