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Publication
PropertyValue
Working Groups Klopstock
SubprojectNone
Open AccessOpen Access Yes
Publication TypeRandomized Controlled Trial
Peer ReviewedYes
PMIDPubMed ID 37268435
DOIDOI 10.1212/WNL.0000000000207402
Publication Year2023
TitleEfficacy and Safety of Elamipretide in Individuals With Primary Mitochondrial Myopathy: The MMPOWER-3 Randomized Clinical Trial.
JournalNeurology
ISSN0028-3878
ESSN1526-632X
URL https://www.ncbi.nlm.nih.gov/pubmed/?term=37268435%5Buid%5D
Pagese238-e252
Issue3
Volume101
Journal AbbreviationNeurology
AuthorsKaraa A, Bertini E, Carelli V, Cohen BH, Enns GM, Falk MJ, Goldstein A, Gorman GS, Haas R, Hirano M, Klopstock T, Koenig MK, Kornblum C, Lamperti C, Lehman A, Longo N, Molnar MJ, Parikh S, Phan H, Pitceathly RDS, Saneto R, Scaglia F, Servidei S, Tarnopolsky M, Toscano A, Van Hove JLK, Vissing J, Vockley J, Finman JS, Brown DA, Shiffer JA, Mancuso M
First AuthorKaraa A
Last AuthorMancuso M