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Publication
PropertyValue
Working Groups Klopstock
SubprojectNone
Open AccessOpen Access Yes
Publication TypeJournal Article
Peer ReviewedYes
PMIDPubMed ID 31055958
DOIDOI 10.1177/1740774519845673
Publication Year2019
TitleThe FOsmetpantotenate Replacement Therapy (FORT) randomized, double-blind, Placebo-controlled pivotal trial: Study design and development methodology of a novel primary efficacy outcome in patients with pantothenate kinase-associated neurodegeneration. Wikidata
JournalClinical trials (London, England)
ISSN1740-7745
ESSN1740-7753
URL https://www.ncbi.nlm.nih.gov/pubmed/?term=31055958%5Buid%5D
Pages410-418
Issue4
Volume16
Journal AbbreviationClin Trials
AuthorsKlopstock T, Escolar ML, Marshall RD, Perez-Dueñas B, Tuller S, Videnovic A, Greblikas F
First AuthorKlopstock T
Last AuthorGreblikas F
ScholiaScholia Wikidata-based representation at Scholia

 External Resources

 Q91766821  Wikidata ID